If you are dealing with hemophilia, leukemia, blindness that’s caused by retinitis pigmentosis, or a severe combined immune deficiency issue, then you might be a viable candidate for this therapy option. a !1AQa"q�2���B#$Rb34�r�C%�S��cs5��&D�TdE£t6�U�e���u��F'���������������Vfv��������7GWgw��������(8HXhx�������� )9IYiy�������� It can work in combination with cell therapy techniques. 11. Although it is not known to cause any disease in humans, it is related to those that can cause colds. The body’s immune system might see the various viruses that we use to replace unwanted genes as invaders that must be extinguished before they cause harm. A number of the clinical studies that are available were based on animal research instead of human subjects. Some protocols utilize both, which can give patients a powerful way to recover from their medical condition. Once returned to the body, the immature cells go to the bone marrow, start maturing, and eventually multiplying to replace all of the defective cells. 9. The body’s immune system might see the various viruses that we use to replace unwanted genes as invaders that must be extinguished before they cause harm. When this disadvantage occurs, then the healthy cells could receive damage that may have unpredictable results. The advantages and disadvantages of gene therapy show that this promising treatment option is potentially useful for some inherited disorders, cancers, and viral infections. 3. The carrier, which is referred to as a vector, receives genetic engineering so that it can perform its job. %PDF-1.2 %���� 10 0 obj << /Length 11 0 R /Filter /FlateDecode >> stream At this point in time, the treatment options for these complex situations is not as refined as it is for those who have a single gene defect. Gene therapies could cause a potential tumor. They can be given intravenously or injected into the specific body tissues that require the extra help. It typically works best in single-gene mutations. There are out-of-body treatment options available. There are funding challenges to consider in this category. There is the possibility that a mutated gene could be inactivated so that its improper functionality stops. The fees for gene therapy can easily exceed $1 million in the United States. �(�,6��6j�. Five of the 30 children who receive gene therapy for their condition went on to develop leukemia. Advantages 5. That means there are over 33 million Americans who could benefit from gene therapy. Gene therapy is based on technology. 3. "#()%$%%! We have already seen how antibiotic resistance changes our approach to medicine. There are a lot of similarities in our DNA that make genetic therapy a possibility. send our content editing team a message here, 19 Advantages and Disadvantages of Free Trade, 18 Advantages and Disadvantages of Homework Should Be Banned, 30 Impressive Sales Manager Resume Objective Statement Examples, 33 Impressive Office Assistant Resume Objective Statement Examples, The 100 Most Asked Salesforce Admin Interview Questions with Answers, The 50 Most Asked Library Assistant Interview Questions with Answers, 125 Thinking of You Text Messages for Him and Her, 40 Ways to Say Thank You for Your Time and Effort, 40 Kind Ways to Say Thank You for Your Advice, The 50 Most Asked School Counselor Interview Questions with Answers, 40 Thank You for the Recognition Messages (via Email or Note), 50 Ways to Say Thank You for Thanksgiving Dinner. Then the results from each study are carefully examined to determine if the risks of the therapy are acceptable when compared to the potential rewards. Ethical concerns about gene therapy exist. New treatment options are coming out all of the time. That’s why tr… One method involves the replacement of a mutated gene with a healthy copy of it. It offers the possibility of a positive medical outcome. Most people would say that the introduction of gene therapy provides several benefits that are worth taking under consideration. 10. The advantages and disadvantages of gene therapy hold the promise to transform medicine as we know it. !>�g_�����3����#"ܪf@�|XdO�ݗݍ?b���/@\�g���H�z_�a"��� �k��4,��� ��O�ij4 �,�����;V�ڱ� o�C����ql�(����M��Rs ez��x�p$�⋩�W�5��bc$R ��j'� 0��6�{����,4��^���H&-ߢiE�a� X�J�*��^ܩ�8dĬ�:x����%��d�wI�X+{:Y]^?�,Ta]��P�������A�ގ��(m:I�\΢��r�!.����VWJ:�!�Q�ŷ�����s�-�'�ŔD���8gf��H�83+�Qy$6�=�A?����� gُ����O�������zc�s`�t$���.l��H�w{4�v�~��v�n�P���e&��ie���h�Z�]���>�s^�v�:�E���8m��I�����2��w㿰q�9�����3���O/��' endstream endobj 11 0 obj 776 endobj 12 0 obj << /Type /XObject /Subtype /Image /Name /I1 /Filter /DCTDecode /Width 75 /Height 75 /BitsPerComponent 8 /ColorSpace /DeviceGray /Length 13 0 R >> stream Researchers are still studying the approach to determine if it is safe and effective for regular use by targeting diseases that have no other cures. '+,,-/4443.4444444444�� K K �� � 7. Birth defects are also potentially preventable with this option, which impacts about 20% of families each year. There are several different approaches to gene therapy being researched today. The focus of gene therapy research is to create new medicines and treatment approaches that can alleviate suffering. These interventions could reduce or eliminate the pain and suffering that occurs when a genetic abnormality is present in a person’s body Almost 4 out of every 5 diseases that adversely impact human health have a genetic foundation to them as well. Some patients might see a limitation in their abilities to conduct the activities of daily living. 2. When the white blood cells attack the newly introduced genetic material, it is not unusual for a patient to experience health issues like inflammation, dizziness, and headaches. We may not have answers to some of these questions until we learn more about the long-term impacts of gene therapy. 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